Research Study – Exercise and Pompe Disease.
Invitation to participate in research for UK adults living with Pompe.
Extension of Early Access to Medicines Scheme for trial Pompe drug.
An update on avalglucosidase alfa.
GSD in the National News.
7 year old twins in Scotland have received their first Covid vaccinations.
Progress on NICE assessment of new treatments.
An update on the appraisal of treatments for Pompe by NICE.
Step-Free Access in London – BBC Politics Show
Jeff Harvey demonstrates the difficulties caused by the lack of step-free access on public transport in London.
Liver Glycogen Storage Disease Top 11 Questions.
The top eleven questions that patients, families and healthcare professionals want to be addressed in liver storage disease by researchers.