Trial: Seroprevalence study in Pompe disease.
The John Walton Muscular Dystrophy Research Centre in Newcastle is running a new study in Pompe disease.
The John Walton Muscular Dystrophy Research Centre in Newcastle is running a new study in Pompe disease.
The Pompe Support Team wanted to create a fun opportunity for children, as a show of support during lockdown.
Spark Therapeutics Announces First Participant Dosed in Phase 1/2 Study of Investigational Gene Therapy for Late-Onset Pompe Disease
Avalglucosidase alfa reaches its first important regulatory milestone
AGSD-UK working with NICE towards approval for new treatment for Pompe disease.
Pompe Support Team’s Medical Overview leaflet is now being used in Australia.