The top eleven questions that patients, families and healthcare professionals want to be addressed in liver storage disease by researchers.
Ultragenyx Announces FDA Clearance of Investigational New Drug (IND) Application for UX053, an mRNA for the Treatment of GSD3
Rob Wood, long time AGSD-UK supporter passes way too soon.
Dr. Weinstein, long-time champion of improved diagnosis and treatment for hepatic GSDs due to move to Passage Bio as VP.
The GSD3 get-together with the CATS at Cudworth Village Hall, on 14 March, has been postponed until later in the year.
Coming up on Saturday 14 March is another get-together for those with GSD3. Bring children, family and friends.