It’s out… Glisten Spring 2020 is here!
The latest edition of our magazine is out. Glisten Spring 2020 is here, packed with news, reports, announcements and information.
GSD3 get-together – 14 March.
Coming up on Saturday 14 March is another get-together for those with GSD3. Bring children, family and friends.
Countdown to Rare Disease Day 2020: 2
Countdown to Rare Disease Day on 29 February. Act now, get involved, it’s easy.
Countdown to Rare Disease Day 2020: 3
Countdown to Rare Disease Day on 29 February. Findacure’s “Drug Repurposing for Rare Diseases” conference returns for its 7th year!
Countdown to Rare Disease Day 2020: 4
2020 is a leap year and Rare Disease Day falls on… Friday 29 February. We are counting down to the day!
Valerion’s trial of therapy for Pompe stopped.
A trial of a new treatment for GSD2 has been halted. VAL-1221 was delivered intravenously in late-onset Pompe patients.