Spark Therapeutics doses the first participant in Gene Therapy trial.
Spark Therapeutics Announces First Participant Dosed in Phase 1/2 Study of Investigational Gene Therapy for Late-Onset Pompe Disease
Spark Therapeutics Announces First Participant Dosed in Phase 1/2 Study of Investigational Gene Therapy for Late-Onset Pompe Disease
Free daily vitamin D supplements are available if you’re at high risk (clinically extremely vulnerable) from coronavirus (COVID-19).
BIMDG have provided a list of frequently asked questions about the vaccination programme for COVID-19
Frank and Irene Green from Altrincham for years have decorated their home with festive lights, this year again raising money for AGSD-UK.
Over the next few months AGSD-UK is offering a series of talks and presentations which will be uploaded each Monday
Has your child been diagnosed with Juvenile Myoclonic Epilepsy?