Countdown to Rare Disease Day 2020: 3
Countdown to Rare Disease Day on 29 February. Findacure’s “Drug Repurposing for Rare Diseases” conference returns for its 7th year!
Countdown to Rare Disease Day 2020: 4
2020 is a leap year and Rare Disease Day falls on… Friday 29 February. We are counting down to the day!
Valerion’s trial of therapy for Pompe stopped.
A trial of a new treatment for GSD2 has been halted. VAL-1221 was delivered intravenously in late-onset Pompe patients.
Christmas lights – a special gift for AGSD-UK.
Frank and Irene Green from Altrincham for years have decorated their home with festive lights, this year raising money for AGSD-UK.
Dr Clive Tonks, ex-committee member of AGSD-UK.
We mark the passing of Dr Clive Tonks in his mid-eighties. He was a past trustee and committee member of AGSD-UK.