International Pompe Day 15 April 2023.
The IPA focused this year’s International Pompe Day on the importance of movement, sharing stories from the community under the slogan “Every Move Counts”.
NICE recommends Avalglucosidase alfa as a treatment option for Pompe.
24th August 2022 The National Institute for Health and Care Excellence today published its recommendation of Avalglucosidase alfa (AVAL) as an option for treating Pompe in babies, children, young people and adults, where AVAL is provided according to the commercial...
Update on NICE assessment of new treatments.
An update on the appraisal of treatments for Pompe by NICE.
International Pompe Day.
International Pompe Day – 15th April 2022
Research Study – Exercise and Pompe Disease.
Invitation to participate in research for UK adults living with Pompe.
Extension of Early Access to Medicines Scheme for trial Pompe drug.
An update on avalglucosidase alfa.