Update on NICE assessment of new treatments.
An update on the appraisal of treatments for Pompe by NICE.
International Pompe Day.
International Pompe Day – 15th April 2022
Research Study – Exercise and Pompe Disease.
Invitation to participate in research for UK adults living with Pompe.
Extension of Early Access to Medicines Scheme for trial Pompe drug.
An update on avalglucosidase alfa.
GSD in the National News.
7 year old twins in Scotland have received their first Covid vaccinations.