Extension of Early Access to Medicines Scheme for trial Pompe drug.
An update on avalglucosidase alfa.
Success for our Benefits Advisor.
AGSD-UK’s Zainib Hussain has been providing much needed support.
GSD in the National News.
7 year old twins in Scotland have received their first Covid vaccinations.
CureGSD1b Research Ready Data Collection Plan.
The CureGSD1b Research Alliance is working extensively on a full understanding of the research landscape related to GSD1b at the moment.
Winter Season 2022
We again will be releasing videos on every Monday of January for our Winter Season.
Progress on NICE assessment of new treatments.
An update on the appraisal of treatments for Pompe by NICE.