Moderna mRNA trial infusion for GSD1a.
First patient receives Moderna mRNA trial infusion for GSD1a.
Gene Therapy Trial for GSD1a Progress.
Trials for a gene therapy treatment for GSD1a are continuing.
CureGSD1b Research Ready Data Collection Plan.
The CureGSD1b Research Alliance is working extensively on a full understanding of the research landscape related to GSD1b at the moment.
Liver Glycogen Storage Disease Top 11 Questions.
The top eleven questions that patients, families and healthcare professionals want to be addressed in liver storage disease by researchers.
Ann Phillips, 1934–2020, co-founder of AGSD-UK.
We are sad to report that AGSD-UK co-founder Ann Phillips has passed away shortly after contracting COVID-19 in her care home. She was 86.
Move for USA-based GSD expert Dr. David Weinstein.
Dr. Weinstein, long-time champion of improved diagnosis and treatment for hepatic GSDs due to move to Passage Bio as VP.