Rare Disease Day 2021
2 days to go until Rare Disease Day 2021.
Eurordis H-Care Survey of rare diseases results.
Eurordis key findings from a survey on patients’ and carers’
experience of medical care for their rare diseases.
Winner announced of the PST Avatar Competition.
The Pompe Support Team wanted to create a fun opportunity for children, as a show of support during lockdown.
Spark Therapeutics doses the first participant in Gene Therapy trial.
Spark Therapeutics Announces First Participant Dosed in Phase 1/2 Study of Investigational Gene Therapy for Late-Onset Pompe Disease
Vitamin D supplements for clinically extremely vulnerable.
Free daily vitamin D supplements are available if you’re at high risk (clinically extremely vulnerable) from coronavirus (COVID-19).
COVID-19 Vaccine FAQ’s.
BIMDG have provided a list of frequently asked questions about the vaccination programme for COVID-19