Research Study – Exercise and Pompe Disease.
Invitation to participate in research for UK adults living with Pompe.
Invitation to participate in research for UK adults living with Pompe.
Trials for a gene therapy treatment for GSD1a are continuing.
New research information has been added to the GSD3 website page.
An update on avalglucosidase alfa.
The CureGSD1b Research Alliance is working extensively on a full understanding of the research landscape related to GSD1b at the moment.
An update on the appraisal of treatments for Pompe by NICE.