101 Top Tips for Pompe disease is now available in Portuguese.
Avalglucosidase-alfa was awarded EAMS (Early Access to Medicines Status) in February 2021.
The John Walton Muscular Dystrophy Research Centre in Newcastle is running a new study in Pompe disease.
The Pompe Support Team wanted to create a fun opportunity for children, as a show of support during lockdown.
Has your child been diagnosed with Juvenile Myoclonic Epilepsy?