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Audentes Pompe Gene Therapy Trial News.

Adult Pompe programme update

Audentes is now enrolling patients in the Phase 1/2 clinical trial to evaluate the investigational gene therapy product candidate in participants who are 18 years or older, ambulatory or non-ambulatory, with late-onset Pompe disease (LOPD).


Clinical trial sites listed

A list of clinical trial sites can be found on the FORTIS page of

FORTIS page with trial details


The page indicates which sites are actively recruiting, currently these are both in the USA, with other countries, including the UK planned.