Countdown to Rare Disease Day 2020: 2
Countdown to Rare Disease Day on 29 February. Act now, get involved, it’s easy.
Countdown to Rare Disease Day 2020: 3
Countdown to Rare Disease Day on 29 February. Findacure’s “Drug Repurposing for Rare Diseases” conference returns for its 7th year!
Countdown to Rare Disease Day 2020: 4
2020 is a leap year and Rare Disease Day falls on… Friday 29 February. We are counting down to the day!
Valerion’s trial of therapy for Pompe stopped.
A trial of a new treatment for GSD2 has been halted. VAL-1221 was delivered intravenously in late-onset Pompe patients.
Happy New Year 2020!
Happy New Year from AGSD-UK to members and friends around the world. Here’s to great progress for GSD in 2020.
Neil Bradbury has stepped down from role of CEO.
The AGSD-UK board of trustees announces that Neil Bradbury has stepped down from his role as Chief Executive Officer.