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Recent news
- Virtual Festive Event. 29th November 2023
- Update on the DTX401 programme for GSD1a. 16th November 2023
- Newborn Genomes Programme. 4th October 2023
- NICE recommends cipaglucosidase alfa plus miglustat. 15th August 2023
- New Continuum of Care Model for McArdle’s. 7th July 2023
- Seminar for people affected by neuromuscular diseases. 17th May 2023
- Main Event 2023 Programme 26th April 2023
- International Pompe Day 15 April 2023. 17th April 2023
- London Marathon 2023. 24th March 2023
- Rare Disease Day 2023. 28th February 2023
- Help Us Raise Awareness. 7th February 2023
- Newsflash – The Main Event 2023 date change! 21st December 2022
- The Main Event 2023. 10th November 2022
- Liberating Research GSD1a Study. 1st November 2022
- McArdle’s walking courses 2023. 24th September 2022