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Recent news
- International Pompe Day. 15th April 2024
- Save the Date! 4th April 2024
- Rare Disease Day 2024. 29th February 2024
- Cipaglucosidase alfa (Pombiliti®) is accepted for use within NHS Scotland. 12th December 2023
- Virtual Festive Event. 29th November 2023
- Update on the DTX401 programme for GSD1a. 16th November 2023
- Newborn Genomes Programme. 4th October 2023
- NICE recommends cipaglucosidase alfa plus miglustat. 15th August 2023
- New Continuum of Care Model for McArdle’s. 7th July 2023
- Seminar for people affected by neuromuscular diseases. 17th May 2023
- Main Event 2023 Programme 26th April 2023
- International Pompe Day 15 April 2023. 17th April 2023
- London Marathon 2023. 24th March 2023
- Rare Disease Day 2023. 28th February 2023
- Help Us Raise Awareness. 7th February 2023