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Recent news
- FDA approves treatment for GSD1a in the U.S. 20th August 2026
- Update on Sanofi supply issues. 18th August 2026
- McArdle walking courses 2026 6th June 2026
- Booking now open for our Main Event 4th-5th July Loughborough. 7th May 2026
- April 15th is International Pompe Day. 15th April 2026
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- Rare Disease Day 2025 28th February 2025
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- International Pompe Day. 15th April 2024
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