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Recent news
- Update on the Beam GSD1a programme. 27th August 2024
- Virtual AGSD-UK support. 21st August 2024
- Update on Spark Therapeutics Pompe gene therapy programme. 23rd July 2024
- Update on phase 3 study of DTX401. 5th June 2024
- International Pompe Day. 15th April 2024
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- Rare Disease Day 2024. 29th February 2024
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- Virtual Festive Event. 29th November 2023
- Update on the DTX401 programme for GSD1a. 16th November 2023
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